Fulcrum Therapeutics

Fulcrum Therapeutics is a company in Cambridge, United States. It launched with a vision to develop small molecules to improve the lives of patients with genetically defined rare diseases in areas of high unmet medical need. The company uses proprietary technology to identify drug targets that can modulate gene expression to treat the known root cause of gene mis-expression. Its lead program, pociredir, is being investigated in clinical trials to treat sickle cell disease (SCD). Alex C. Sapir serves as President and Chief Executive Officer and Board Member.

Fulcrum Therapeutics launched with a vision to develop small molecules to improve the lives of patients with genetically defined rare diseases in areas of high unmet medical need. The company uses proprietary technology to identify drug targets that can modulate gene expression to treat the known root cause of gene mis-expression. Its lead program, pociredir, is being investigated in clinical trials to treat sickle cell disease (SCD).

Focused on improving the lives of patients with genetically defined diseases in areas of high unmet medical need.

• pociredir

  Lead program being investigated in clinical trials to treat sickle cell disease (SCD).

1. 1Fulcrum Therapeuticsfulcrumtx.com
2. 2About • Fulcrum Therapeuticsfulcrumtx.com
3. 3Therapeutic Focus • Fulcrum Therapeuticsfulcrumtx.com
4. 4Fulcrum Therapeutics (United States)wikidata.org